---
title: Rare Disease CDMOs
path: /indications/rare-disease
companies_count: 15
---

# Rare Disease CDMOs

15 published CDMOs match Rare Disease.

Locations in this set include United States, China, United Kingdom, Brazil, France, and India.

Capabilities that show up most often in this set: CMC Analytical Development, Process Development, CMC Regulatory Submission Support, Technology Transfer, and Quality Control Testing.

## Matching companies

- [Aldevron](/companies/aldevron)
  - Aldevron is a CDMO specializing in mRNA manufacturing with LNP encapsulation and fill/finish, viral vector production, plasmid DNA, and gene therapy solutions from discovery through commercialization.
- [Andelyn Biosciences](/companies/andelynbio)
  - CDMO specializing in plasmid DNA and AAV viral vector manufacturing for cell and gene therapy, with digital-first platform emphasizing data integrity and collaboration.
- [AskBio](/companies/askbio)
  - AskBio is a clinical-stage gene therapy company developing AAV gene therapies for genetic and rare disorders, with a focus on advancing genetic technology and lowering production costs to increase patient access.
- [Cell and Gene Therapy Catapult](/companies/ct)
  - UK-based innovation and manufacturing support organization for cell and gene therapies, offering infrastructure, expertise, and collaboration across the ATMP lifecycle.
- [Cytovance Biologics](/companies/cytovance-biologics)
  - U.S.-based CDMO offering end-to-end biomanufacturing services for antibodies, recombinant proteins, vaccines, and other biologics modalities, with dedicated microbial and mammalian facilities and in-house cell line development capabilities.
- [ElevateBio](/companies/elevate)
  - Advanced therapies CDMO providing discovery, process development, manufacturing, and regulatory support for cell therapies, viral vectors, mRNA, and gene editing programs from preclinical through commercial scale.
- [Forge Biologics](/companies/forgebiologics)
  - Dedicated AAV gene therapy CDMO with a 200,000+ sq. ft. cGMP facility featuring 20 suites and bioreactors up to 5,000L, supporting 60+ clients across 35+ indications with high-yield manufacturing and seamless regulatory compliance.
- [LGC Biosearch Technologies](/companies/biosearchtech)
  - GMP-compliant manufacturer of custom oligos, qPCR probes, and diagnostic kits for infectious diseases, oncology, and prenatal testing; ISO 13485-certified for clinical and diagnostic markets.
- [Maravai LifeSciences](/companies/maravai)
  - Leading provider of nucleic acid products, custom enzymes, and bioprocess analytics supporting vaccine, therapeutic, and diagnostic development from discovery through commercialization, with mRNA CDMO services including proprietary CleanCap® capping technology.
- [Pharmaron](/companies/pharmaron)
  - Premier life science CRO and CDMO offering integrated R&D and manufacturing across drug discovery, preclinical, clinical development, and commercialization for small molecules, biologics, and cell & gene therapies. 25,000+ employees across China, US, and UK.
- [Scinai Immunotherapeutics Ltd.](/companies/scinai-immunotherapeutics)
  - Boutique biologics CDMO providing analytical method development, process development, and cGMP manufacturing for biotech clients from early research through Phase 3, backed by over 20 years of experience and state-of-the-art facilities.
- [Stason Industrial Corporation](/companies/stasonpharma)
  - US-based CDMO offering contract packaging, analytical testing, and manufacturing services for clinical trial and commercial pharmaceutical production, with specialized high-containment capabilities for potent compounds.
- [Syngene International](/companies/syngeneintl)
  - Innovation-led CRDMO offering integrated scientific services from early discovery through commercial manufacturing, with cGMP-compliant facilities, 5,200+ scientists, and a new 50,000-liter single-use bioreactor capacity in the U.S.
- [Unither Pharmaceuticals](/companies/unither-pharma)
  - Global CDMO specializing in sterile and non-sterile liquid manufacturing, including Blow-Fill-Seal (BFS) single-dose technology with over 5 billion annual capacity, plus formulation development, analytical services, and ophthalmic expertise across six production sites.
- [Viralgen](/companies/viralgen)
  - Viralgen is a CDMO specializing exclusively in cGMP AAV gene therapy manufacturing, with the world's largest dedicated AAV production capacity and a 100% success rate for IND/IMPD dossiers across 50+ gene therapy customers.